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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Epigenetics
Muscles/physiopathology
Becker muscular dystrophy BMD
Molecular Sequence Data
Duchenne muscular dystrophy
CTNNB1
Diseases
Activin Receptors
Gene Expression Regulation/drug effects
Becker muscular dystrophy
Génomique
Duchenne DMD dystrophy
Dystrophie Musculaire de Duchenne DMD
Human Umbilical Vein Endothelial Cells
Long QT
Dynamin 2
Dystrophin-EGFP
LncRNA
Animal/physiopathology
Dystrophin central domain
LncARN
DMO
Inbred C57BL
Cardiomyopathie
Delivery
DHPR α1S
Animals
Cardiomyopathy
Energy Metabolism/drug effects
Mice
Multi resolution modeling
Immunoglobulin Fc Fragments/pharmacology
Humans
Mdx mouse
Dystrophie Musculaire de Becker BMD
LKB1
L-Type
NNOS
Invivo
Autophagy
Modificateurs de gènes
Dystrophin
Molecular docking
Inhibitors
Metabolism
Genomic
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Dystrophie musculaire de Becker
Homeostasis
Base Sequence
Male
Long noncoding RNA
Cell Biology
Mitochondrial fission
Becker BMD muscular dystrophy
Calcium Channels
Clinical trials
Liver
Muscle Strength
Myotendinous junction
Myogenesis
Inbred mdx
Morphogenesis
Hear
Cell homeostasis
Muscular Atrophy
MES
Duchenne muscular dystrophy DMD
Skeletal muscle
Calcium
Multi exon skipping
BMD
Cultured
Muscular dystrophy
Drp1
NAD+
Muscle development
Cells
CaV subunits
Muscle
Multiresolution modeling
Cell Line
Cachexia
CaVβs
Dystrophine
DMD
Ex-vivo
Muscle Biology
Knockout
Muscular Dystrophy
MiARN
Antisense oligonucleotides
Exon skipping
Gene expression
Gene modifiers
Allele‐specific silencing therapy
Dystrophy
Hepatocellular carcinoma
CD38
Centronuclear myopathy